Bill Vick

This study is a randomized, placebo-controlled study, testing an investigational medicine called ARCT-810 on adults with ornithine transcarbamylase (OTC) deficiency.

Disorder of urea cycle metabolism and ammonia detoxification

Ornithine transcarbamylase (OTC) deficiency clinical research study

Take part in a study about the everyday experiences of people who are living with generalized myasthenia gravis (gMG)! (Adult caregivers may answer on behalf of people with gMG.)

Myasthenia gravis

Study into living with generalized myasthenia gravis: Part 1

This study aims to learn what people with cystic fibrosis actually think about taking the CFTR modulator therapies Kalydeco, Orkambi, Symdeko/Symkevi, and Trikafta/Kaftrio. This is not like other studies that may only focus on following doctors’ orders.

Cystic fibrosis

What do you think about your cystic fibrosis treatment(s)?

Pravin Pant

This placebo-controlled Phase 3 study is testing an investigational medicine called ravulizumab-cwvz, also known in this study as ALXN1210, on adults with anti-AChR antibody-positive, generalized myasthenia gravis (gMG).

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